With a progressive disease like FSHD, the loss of abilities and independence has an unpredictable timeline, says columnist.
The firm at the JP Morgan Healthcare Conference additionally expects a regulatory decision on its gene therapy RGX-121 for Hunter syndrome next month.
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Full list of medical conditions you must declare to DVLA
Drivers could face up to £1,000 fines and potential prosecution if they fail to report notifiable medical conditions or ...
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