Nebraska families and advocates gathered to protest proposed cuts to family caregiving hours, fearing the changes could force ...

The firm at the JP Morgan Healthcare Conference additionally expects a regulatory decision on its gene therapy RGX-121 for Hunter syndrome next month.

Society columnist Bruce Cook writes this week about two Orange County-based nonprofits that celebrated the holidays in style ...

Three current members of Florida State University’s Board of Trustees, all alumni, will remain on the panel. Here's how.

Solid Biosciences (SLDB) stock rises as a Phase 1/2 trial for its lead asset SGT-003 in Duchenne muscular dystrophy reaches ...

In research published in Developmental Medicine & Child Neurology, investigators developed a brief, reliable, and valid screening tool to help identify individuals with Duchenne muscular dystrophy (a ...

The Muscular Dystrophy Association (MDA) is proud to announce the recipients of the 2026 MDA Legacy Awards, recognizing excellence in scientific and clinical research and saluting outstanding ...

In research published in Developmental Medicine & Child Neurology, investigators have developed a brief, reliable, and valid ...

It will be held on Jan. 24 at the Dobson Ranch Golf Course in Mesa. Activities include Beat the Pro, 50/50 Raffle, Closest to ...

Jefferies analysts forecast a $1 billion market opportunity for each of Sarepta’s siRNA programs for facioscapulohumeral ...

A stretch of viral DNA in the mouse genome gives cells in early-stage embryos the potential to become almost any cell type in ...

PPMD extends its heartfelt thanks to all Race to End Duchenne runners, donors, and volunteers who made the 2026 Walt Disney World (R) Marathon Weekend a memorable and meaningful success. To learn more ...